27-11-2024 01:02 via drugs.com

FDA Approves Kebilidi for Aromatic L-Amino Acid Decarboxylase Deficiency

TUESDAY, Nov. 26, 2024-- The U.S. Food and Drug Administration has approved Kebilidi (eladocagene exuparvovec-tneq) for the treatment of adult and pediatric patients with aromatic L-amino acid decarboxylase (AADC) deficiency.The adeno-associated...
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