19-07-2018 17:00 via theverge.com

Scientists treated a mouse’s genetic disorder in the womb — here’s what’s next

This week, scientists reported that they were able to treat a serious genetic disorder in the womb — in mice. It sounds like science fiction, but this type of treatment may not be far away for humans. What will we need to figure out before we get there?For the study published in Nature Medicine, scientists studied the neurodegenerative disorder Gaucher syndrome. Gaucher is caused by mutations in the GBA gene and leads to serious joint pain, convulsions, and cognitive impairment. To treat
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