24-12-2025 18:19 via medpagetoday.com

FDA Approves Mitapivat for Thalassemia-Related Anemia

(MedPage Today) -- The FDA approved mitapivat (Aqvesme) as a disease-modifying treatment for anemia in adults with alpha- or beta-thalassemia, a rare inherited blood disease that affects hemoglobin production.
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