It Starts with One (Rare) Patient

In 1983, patient advocates – now known as the National Organization for Rare Disease, NORD – ignited a movement and rallied support  for the Orphan Drug Act to facilitate development of treatments for conditions affecting fewer than 200,00 Americans.  It started with this one idea and served as the catalyst to ignite a new generation of enhanced support, advocacy and treatments for rare disease patients.
Today, there are hundreds of patient advocacy groups, more than 770 ne