Gene-Therapy Trials for Inherited Form of Blindness Could Start in Two Years

Scientists in the U.S. say human trials of gene therapy for an inherited form of blindness known as vitelliform macular degeneration, or Best disease, could be less than two years away, following successful use of the treatment in a canine model of the disease. Developed through a longstanding collaboration between scientists at the University of Pennsylvania’s School of Veterinary Medicine and Penn’s Perelman School of Medicine, the canine therapy, which involves injections of a hea